- Investigator
- Sandeep Grover
- Ages
- 12 Years - 50 Years
- Sexes
- Male
Clinical trials
-
A Phase 2/3, Randomized, Controlled, Masked, Multi-center Study to Evaluate the Efficacy, Safety and Tolerability of Two Doses of AGTC-501, a Recombinant Adeno-associated Virus Vector Expressing RPGR (rAAV2tYF-GRK1-RPGR), Compared to an Untreated Control -
A Natural History and Outcome Measure Discovery Study of PRPF31 Mutation–Associated Retinal Dystrophy (20226317) - Investigator
- Sandeep Grover
- Ages
- N/A
- Sexes
- All
-
A Randomized Clinical Trial Evaluating Fenofibrate for Prevention of Diabetic Retinopathy Worsening (Protocol AF) - Investigator
- Sandeep Grover
- Ages
- N/A
- Sexes
- All
-
Biobank for Potential or Known Genetic Diseases - Investigator
- Pamela L Trapane
- Ages
- 0 Years - 100 Years
- Sexes
- All
-
Rare Disease Registry - Investigator
- Pamela L Trapane
- Ages
- 0 Years - 100 Years
- Sexes
- All
-
A Global Prospective Observational Registry of Patients with Pompe Disease - Investigator
- Pamela L Trapane
- Ages
- 0 Years - 100 Years
- Sexes
- All
-
An Open-label Extension Study of Inhaled Treprostinil in Subjects with Fibrotic Lung Disease (20212063) - Investigator
- Vandana K Seeram
- Ages
- 40 Years - 99 Years
- Sexes
- All
-
The MAGICAL SV Randomized Clinical Trial - Investigator
- Daniel E Soffer
- Ages
- 18 Years - 99 Years
- Sexes
- All
-
STOMP study - Investigator
- Mobeen H Rathore
- Ages
- 7 Years - 60 Years
- Sexes
- All